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Hemochromatosis Therapeutics Pipeline to Witness Significant Growth due to Positive Clinical Results in the Coming Years

According to a new research report Hemochromatosis Therapeutics – Competitive Landscape, Epidemiology Forecast, and Pipeline Analysis, 2019” published by Pharma Proff, hemochromatosis/iron overload therapeutics currently exhibits a proliferating pipeline with 10+ therapeutic candidates.

Hemochromatosis Therapeutics Pipeline Insights

Hemochromatosis, also known as iron overload, is identified as increased level of iron in the body. It has symptoms such as joint pain, weight loss, erectile dysfunction in men, and irregular menstrual cycle in women. Hemochromatosis can be categorized into two types: primary hemochromatosis and secondary hemochromatosis. Primary hemochromatosis is genetic disorder; however, secondary hemochromatosis occurs due to medical conditions such as anemia, thalassemia, and others.

If hemochromatosis is not diagnosed or treated at an early stage, it may lead to some serious complications such as liver damage, diabetes, arthritis, reproductive complications, and cardiovascular diseases. The commonly used diagnostic techniques are blood test, and physical examination. Additional liver function test (LFT), magnetic resonance imaging (MRI), and liver biopsy procedures are performed to confirm the disease.

Exjade by Novartis International AG, and Ferriprox by ApoPharma Inc. are the two key U.S. Food and Drug Administration (USFDA) approved drugs for the treatment of hemochromatosis.

Insights into Pipeline Segments

According to the research findings, majority of pipeline drug candidates are being developed for oral administration. It has been observed that oral route of medications is convenient, available in delayed or rapid release formulation, less risk of systemic infections, and inexpensive in nature, and also provides improved patient’s compliance. Administration of therapeutics for hemochromatosis through the oral route has shown promising results in clinical studies.

Positive Clinical Trial Results are Expected to Drive Hemochromatosis Therapeutics Pipeline

Companies that are involved in developing therapeutics for hemochromatosis have shown positive clinical results in various phases of drug development. For instance, in September 2016, La Jolla Pharmaceutical Company demonstrated positive results from a phase I study of LJPC-401 in patients with hereditary hemochromatosis, thalassemia, and sickle cell diseases. Results of the study were positive as LJPC-401 was well-tolerated with no dose limiting toxicities. Furthermore, in March 2019, La Jolla Pharmaceutical Company announced in its financial report that topline results of LJPC-401 in patients with hereditary hemochromatosis are expected in second half of 2019.

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Global Market for Hemochromatosis Therapeutics is Expected to Increase Statistically in the next 10 years

As of 2018, Exjade and Ferriprox are two marketed products available in the market for the treatment of hemochromatosis. Due to emergence of late- and mid-stage pipeline products, the overall hemochromatosis therapeutics market is expected to grow significantly in the upcoming years.

Novartis International AG, ApoPharma Inc., La Jolla Pharmaceutical Company, DisperSol Technologies, Silence Therapeutics plc, and Vifor Pharma Management Ltd. are some of the key companies involved in the development of drug candidates for the treatment of hemochromatosis.

Hemochromatosis Therapeutics Pipeline Analysis

  • By Phase
  • By Molecule Type
  • By Route of Administration
  • By Company

This report comprises detailed pipeline analysis of therapeutics being developed for the treatment of hemochromatosis. Comprehensive insights of the pipeline phase products have been provided with special focus on strategic development activities, inclusive of collaboration and licensing information, drug designations, financing, grants, technological advancements, patents, and upcoming conferences. In addition, the report highlights the winning strategies of companies involved in the hemochromatosis therapeutics development. Detailed regulatory approval procedures in the U.S., Europe, and Japan are also provided in this report. Furthermore, the report contains competitive analysis and extensive information on monotherapies, combination therapies, targets and mechanism of action, and drug origin with relevance to hemochromatosis.